FDA Approves First Treatment for Hutchinson-Gilford Progeria Syndrome and Some Progeroid Laminopathies
Decades of NIH research helped lead to the first FDA-approved treatment for progeria. NIH Director Francis S. Collins, M.D., Ph.D., available to discuss this major advance for the rare, fatal pediatric disease, his lab’s research activities on progeria, including its involvement in the discovery of the gene responsible for the disease, the development of a …